A Science (New York, N.Y.) - Science 2026 (Pubmed ID 41643021)

syn75139650

Created By Synapse-Service-AD-Data-Curation-01 synapse-service-ad-data-curation-01

DOI: 10.1126/science.adv2600
year: 2026
grant: R01AG058063
title: Blocking RAN translation without altering repeat RNAs rescues <i>C9ORF72</i>-related ALS and FTD phenotypes.
Program: ACTDRx AD
authors: A A Quadros AR Aguilar C Albers MW Arnold SE Aryal S Basu H Beaussant HDAM Canori M Castellanos Otero P Chiu IM Da Costa P Daughrity LM Eriani G Gao FB Griesman G Held A Hruska-Plochan M Jain A Jansen-West K Jiang X Krishnan G Lagier-Tourenne C Lee CZ Lim SM Lopez-De-Silanes ES Marques C Martin F Moran LC Nolan M Patni D Petrucelli L Polymenidou M Ramesh N Ray-Soni A Reyes CJF Russo T Schaeffer L Song Y Takakuwa H Trombetta BA Vieira Souza Da Silva Y Wainger BJ Wheeler H Wymann B Yue M Zhang YJ
journal: Science (New York, N.Y.) - Science
pubmed_id: 41643021

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