title: ADVL1521 Omic Data Repository funder: NIH-NCI creator: Kevin Shannon Mignon Loh license: UNKNOWN species: Homo sapiens studyId: syn51133946 subject: Juvenile myelomonocytic leukemia Ras signaling MEK inhibition Trametinib dataType: gene expression keywords: juvenile myelomonocytic leukemia MEK inhibitor trametinib single-cell RNA-seq accessType: Controlled Access contributor: University of California, San Francisco description: Single-cell RNA sequencing data from the ADVL1521 clinical trial evaluating the MEK inhibitor trametinib in children with juvenile myelomonocytic leukemia (JMML). Data includes pre- and post-treatment samples. diseaseFocus: Neurofibromatosis type 1 manifestation: Juvenile Myelomonocytic Leukemia (JMML) specimenCount: 14 individualCount: 7 dataUseModifiers: General Research Use measurementTechnique: single-cell RNA-seq